
▲ 9 r/FSHD
Dyne theraputics in preclinical development for FSHD cure
No active study to enroll into yet, but worth keeping an eye on (pre-clinical)
u/Fancy-Supermarket-73 — 6 days ago

No active study to enroll into yet, but worth keeping an eye on (pre-clinical)
To my fellow FSHDers, some good news—unless someone else has already posted it.
The main link worth reading:
https://investorrelations.sarepta.com/static-files/7de668c5-4a60-440c-8dd9-22884fd57703
It absolutely blows Avidity’s intracellular concentration and DUX4 reduction results out of the water.
Phase 2 enrolment is expected to begin in late 2026 (october) or early 2027:
https://www.sarepta.com/community-letter-update-fshd1-clinical-development-program